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Authors
- Alrawi, Zayd
- Bryda, Elizabeth C
- Davis, Daniel
- Ebert, Allison D
- Hopkins, Abigail E
- Kacher, Mona
- Kaifer, Kevin A
- Lorson, Christian L
- Marquez, Jose
- Neff, Rachel
- O'Brien, Benjamin S
- O'Day, Siri
- Rindt, Hansjörg
- Shababi, Monir
- Simon, Madeline E
- Sison, Samantha L
- Smith, Caley E
- Villalón, Eric
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Topics
- Animals
- CRISPR-Cas Systems
- DNA-Binding Proteins
- Dependovirus
- Disease Models, Animal
- Down-Regulation
- Female
- Genetic Vectors
- Humans
- Induced Pluripotent Stem Cells
- Male
- Mice
- Mice, Inbred Strains
- MicroRNAs
- Motor Neurons
- Muscle, Skeletal
- Muscular Atrophy, Spinal
- Neuromuscular Junction
- genetics
- metabolism
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