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Exon-specific U1 snRNAs improve ELP1 exon 20 definition and rescue ELP1 protein expression in a familial dysautonomia mouse model. [electronic resource] by
- Donadon, Irving
- Pinotti, Mirko
- Rajkowska, Katarzyna
- Pianigiani, Giulia
- Barbon, Elena
- Morini, Elisabetta
- Motaln, Helena
- Rogelj, Boris
- Mingozzi, Federico
- Slaugenhaupt, Susan A
- Pagani, Franco
Producer: 20190312
In:
Human molecular genetics vol. 27
Availability: No items available.
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Rescue of spinal muscular atrophy mouse models with AAV9-Exon-specific U1 snRNA. [electronic resource] by
- Donadon, Irving
- Bussani, Erica
- Riccardi, Federico
- Licastro, Danilo
- Romano, Giulia
- Pianigiani, Giulia
- Pinotti, Mirko
- Konstantinova, Pavlina
- Evers, Melvin
- Lin, Shuo
- Rüegg, Markus A
- Pagani, Franco
Producer: 20191209
In:
Nucleic acids research vol. 47
Availability: No items available.
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