Results
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K14 mRNA reprogramming for dominant epidermolysis bullosa simplex. [electronic resource] by
- Wally, Verena
- Brunner, Marietta
- Lettner, Thomas
- Wagner, Martin
- Koller, Ulrich
- Trost, Andrea
- Murauer, Eva M
- Hainzl, Stefan
- Hintner, Helmut
- Bauer, Johann W
Producer: 20110510
In:
Human molecular genetics vol. 19
Availability: No items available.
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13.
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Trans-splicing improvement by the combined application of antisense strategies. [electronic resource] by
- Koller, Ulrich
- Hainzl, Stefan
- Kocher, Thomas
- Hüttner, Clemens
- Klausegger, Alfred
- Gruber, Christina
- Mayr, Elisabeth
- Wally, Verena
- Bauer, Johann W
- Murauer, Eva M
Producer: 20150914
In:
International journal of molecular sciences vol. 16
Availability: No items available.
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14.
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A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair. [electronic resource] by
- Peking, Patricia
- Koller, Ulrich
- Hainzl, Stefan
- Kitzmueller, Sophie
- Kocher, Thomas
- Mayr, Elisabeth
- Nyström, Alexander
- Lener, Thomas
- Reichelt, Julia
- Bauer, Johann W
- Murauer, Eva M
Producer: 20160301
In:
Molecular therapy. Nucleic acids vol. 5
Availability: No items available.
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15.
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A novel screening system improves genetic correction by internal exon replacement. [electronic resource] by
- Koller, Ulrich
- Wally, Verena
- Mitchell, Lloyd G
- Klausegger, Alfred
- Murauer, Eva M
- Mayr, Elisabeth
- Gruber, Christina
- Hainzl, Stefan
- Hintner, Helmut
- Bauer, Johann W
Producer: 20111122
In:
Nucleic acids research vol. 39
Availability: No items available.
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16.
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RNA Trans-Splicing Modulation via Antisense Molecule Interference. [electronic resource] by
- Liemberger, Bernadette
- Piñón Hofbauer, Josefina
- Wally, Verena
- Arzt, Claudia
- Hainzl, Stefan
- Kocher, Thomas
- Murauer, Eva M
- Bauer, Johann W
- Reichelt, Julia
- Koller, Ulrich
Producer: 20180827
In:
International journal of molecular sciences vol. 19
Availability: No items available.
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17.
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18.
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COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa. [electronic resource] by
- Hainzl, Stefan
- Peking, Patricia
- Kocher, Thomas
- Murauer, Eva M
- Larcher, Fernando
- Del Rio, Marcela
- Duarte, Blanca
- Steiner, Markus
- Klausegger, Alfred
- Bauer, Johann W
- Reichelt, Julia
- Koller, Ulrich
Producer: 20180614
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 25
Availability: No items available.
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19.
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An RNA-targeted therapy for dystrophic epidermolysis bullosa. [electronic resource] by
- Peking, Patricia
- Koller, Ulrich
- Duarte, Blanca
- Murillas, Rodolfo
- Wolf, Susanne
- Maetzig, Tobias
- Rothe, Michael
- Kocher, Thomas
- García, Marta
- Brachtl, Gabriele
- Schambach, Axel
- Larcher, Fernando
- Reichelt, Julia
- Bauer, Johann W
- Murauer, Eva M
Producer: 20171128
In:
Nucleic acids research vol. 45
Availability: No items available.
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20.
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Closure of a Large Chronic Wound through Transplantation of Gene-Corrected Epidermal Stem Cells. [electronic resource] by
- Bauer, Johann W
- Koller, Josef
- Murauer, Eva M
- De Rosa, Laura
- Enzo, Elena
- Carulli, Sonia
- Bondanza, Sergio
- Recchia, Alessandra
- Muss, Wolfgang
- Diem, Anja
- Mayr, Elisabeth
- Schlager, Pamina
- Gratz, Iris K
- Pellegrini, Graziella
- De Luca, Michele
Producer: 20180716
In:
The Journal of investigative dermatology vol. 137
Availability: No items available.
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