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	1.	Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector. [electronic resource] by Wang, Lili Wang, Huan Bell, Peter McMenamin, Deirdre Wilson, James M Producer: 20121005 In: Human gene therapy vol. 23 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	2.	Alternative Start Sites Downstream of Non-Sense Mutations Drive Antigen Presentation and Tolerance Induction to C-Terminal Epitopes. [electronic resource] by Ashley, Scott N Somanathan, Suryanarayan Hinderer, Christian Arias, Maxwell McMenamin, Deirdre Draper, Christine Wilson, James M Producer: 20170927 In: Journal of immunology (Baltimore, Md. : 1950) vol. 198 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	3.	Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome. [electronic resource] by Wang, Lili Morizono, Hiroki Lin, Jianping Bell, Peter Jones, David McMenamin, Deirdre Yu, Hongwei Batshaw, Mark L Wilson, James M Producer: 20120723 In: Molecular genetics and metabolism vol. 105 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	4.	Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids. [electronic resource] by Wang, Lili Bell, Peter Somanathan, Suryanarayan Wang, Qiang He, Zhenning Yu, Hongwei McMenamin, Deirdre Goode, Tamara Calcedo, Roberto Wilson, James M Producer: 20160927 In: Molecular therapy : the journal of the American Society of Gene Therapy vol. 23 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	5.	Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome. [electronic resource] by Greig, Jenny A Nordin, Jayme M L Draper, Christine McMenamin, Deirdre Chroscinski, Edward A Bell, Peter Gray, John T Richman, Laura K Wilson, James M Publication details: Molecular therapy. Methods & clinical development Sep 2018 In: Molecular therapy. Methods & clinical development vol. 10 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	6.	CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice. [electronic resource] by Wang, Lili Yang, Yang Breton, Camilo Ayala White, John Zhang, Jia Che, Yan Saveliev, Alexei McMenamin, Deirdre He, Zhenning Latshaw, Caitlin Li, Mingyao Wilson, James M Producer: 20200109 In: Blood vol. 133 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	7.	A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice. [electronic resource] by Yang, Yang Wang, Lili Bell, Peter McMenamin, Deirdre He, Zhenning White, John Yu, Hongwei Xu, Chenyu Morizono, Hiroki Musunuru, Kiran Batshaw, Mark L Wilson, James M Producer: 20160801 In: Nature biotechnology vol. 34 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	8.	Biodistribution of AAV8 vectors expressing human low-density lipoprotein receptor in a mouse model of homozygous familial hypercholesterolemia. [electronic resource] by Chen, Shu-Jen Sanmiguel, Julio Lock, Martin McMenamin, Deirdre Draper, Christine Limberis, Maria P Kassim, Sadik H Somanathan, Suryanarayan Bell, Peter Johnston, Julie C Rader, Daniel J Wilson, James M Producer: 20140925 In: Human gene therapy. Clinical development vol. 24 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	9.	A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency. [electronic resource] by Wang, Lili Yang, Yang Breton, Camilo Bell, Peter Li, Mingyao Zhang, Jia Che, Yan Saveliev, Alexei He, Zhenning White, John Latshaw, Caitlin Xu, Chenyu McMenamin, Deirdre Yu, Hongwei Morizono, Hiroki Batshaw, Mark L Wilson, James M Producer: 20201111 In: Science advances vol. 6 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	10.	Adeno-associated virus-mediated expression of human butyrylcholinesterase to treat organophosphate poisoning. [electronic resource] by Gupta, Vibhor Cadieux, C Linn McMenamin, Deirdre Medina-Jaszek, C Angelica Arif, Muhammad Ahonkhai, Omua Wielechowski, Erik Taheri, Maryam Che, Yan Goode, Tamara Limberis, Maria P Li, Mingyao Cerasoli, Douglas M Tretiakova, Anna P Wilson, James M Producer: 20200316 In: PloS one vol. 14 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)