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	1.	Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes. [electronic resource] by McClements, Michelle E MacLaren, Robert E Producer: 20180719 In: The Yale journal of biology and medicine vol. 90 Availability: No items available. Save to lists Add to cart (remove)
	2.	Gene therapy for retinal disease. [electronic resource] by McClements, Michelle E MacLaren, Robert E Producer: 20130508 In: Translational research : the journal of laboratory and clinical medicine vol. 161 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	3.	A fragmented adeno-associated viral dual vector strategy for treatment of diseases caused by mutations in large genes leads to expression of hybrid transcripts. [electronic resource] by McClements, Michelle E Charbel Issa, Peter Blouin, Véronique MacLaren, Robert E Publication details: Journal of genetic syndromes & gene therapy Nov 2016 In: Journal of genetic syndromes & gene therapy vol. 7 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	4.	CRISPR Interference-Potential Application in Retinal Disease. [electronic resource] by Peddle, Caroline F Fry, Lewis E McClements, Michelle E MacLaren, Robert E Producer: 20210105 In: International journal of molecular sciences vol. 21 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	5.	The Location of Exon 4 Mutations in RP1 Raises Challenges for Genetic Counseling and Gene Therapy. [electronic resource] by Nanda, Anika McClements, Michelle E Clouston, Penny Shanks, Morag E MacLaren, Robert E Producer: 20200124 In: American journal of ophthalmology vol. 202 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	6.	Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina. [electronic resource] by Patrício, Maria I Barnard, Alun R Orlans, Harry O McClements, Michelle E MacLaren, Robert E Publication details: Molecular therapy. Nucleic acids Mar 2017 In: Molecular therapy. Nucleic acids vol. 6 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	7.	RNA editing as a therapeutic approach for retinal gene therapy requiring long coding sequences. [electronic resource] by Fry, Lewis E Peddle, Caroline F Barnard, Alun R McClements, Michelle E MacLaren, Robert E Producer: 20201105 In: International journal of molecular sciences vol. 21 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	8.	Molecular Strategies for RPGR Gene Therapy. [electronic resource] by Cehajic Kapetanovic, Jasmina McClements, Michelle E Martinez-Fernandez de la Camara, Cristina MacLaren, Robert E Producer: 20200116 In: Genes vol. 10 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	9.	An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult [electronic resource] by McClements, Michelle E Barnard, Alun R Singh, Mandeep S Charbel Issa, Peter Jiang, Zhichun Radu, Roxana A MacLaren, Robert E Producer: 20200312 In: Human gene therapy vol. 30 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	10.	Repair of Retinal Degeneration following Ex Vivo Minicircle DNA Gene Therapy and Transplantation of Corrected Photoreceptor Progenitors. [electronic resource] by Barnea-Cramer, Alona O Singh, Mandeep Fischer, Dominik De Silva, Samantha McClements, Michelle E Barnard, Alun R MacLaren, Robert E Producer: 20201225 In: Molecular therapy : the journal of the American Society of Gene Therapy vol. 28 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	11.	A Novel Achromatopsia Mouse Model Resulting From a Naturally Occurring Missense Change in Cngb3. [electronic resource] by Hassall, Mark M Barnard, Alun R Orlans, Harry O McClements, Michelle E Charbel Issa, Peter Aslam, Sher A MacLaren, Robert E Producer: 20190524 In: Investigative ophthalmology & visual science vol. 59 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	12.	Clinical and Molecular Characterization of PROM1-Related Retinal Degeneration. [electronic resource] by Cehajic-Kapetanovic, Jasmina Birtel, Johannes McClements, Michelle E Shanks, Morag E Clouston, Penny Downes, Susan M Charbel Issa, Peter MacLaren, Robert E Producer: 20200218 In: JAMA network open vol. 2 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	13.	Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues. [electronic resource] by Chandler, Laurel C Barnard, Alun R Caddy, Sarah L Patrício, Maria I McClements, Michelle E Fu, Howell Rada, Cristina MacLaren, Robert E Xue, Kanmin Publication details: Molecular therapy. Methods & clinical development Sep 2019 In: Molecular therapy. Methods & clinical development vol. 14 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	14.	AAV2/8 Anti-angiogenic Gene Therapy Using Single-Chain Antibodies Inhibits Murine Choroidal Neovascularization. [electronic resource] by Hughes, Chris P O'Flynn, Neil M J Gatherer, Maureen McClements, Michelle E Scott, Jennifer A MacLaren, Robert E Goverdhan, Srinivas Glennie, Martin J Lotery, Andrew J Publication details: Molecular therapy. Methods & clinical development Jun 2019 In: Molecular therapy. Methods & clinical development vol. 13 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	15.	Function of human pluripotent stem cell-derived photoreceptor progenitors in blind mice. [electronic resource] by Barnea-Cramer, Alona O Wang, Wei Lu, Shi-Jiang Singh, Mandeep S Luo, Chenmei Huo, Hongguang McClements, Michelle E Barnard, Alun R MacLaren, Robert E Lanza, Robert Producer: 20180530 In: Scientific reports vol. 6 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	16.	A Quantitative Chloride Channel Conductance Assay for Efficacy Testing of AAV.BEST1. [electronic resource] by Wood, Shaun R McClements, Michelle E Martinez-Fernandez de la Camara, Cristina Patrício, Maria I Uggenti, Carolina Sekaran, Sumathi Barnard, Alun R Manson, Forbes D MacLaren, Robert E Producer: 20200316 In: Human gene therapy methods vol. 30 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	17.	Codon-Optimized RPGR Improves Stability and Efficacy of AAV8 Gene Therapy in Two Mouse Models of X-Linked Retinitis Pigmentosa. [electronic resource] by Fischer, M Dominik McClements, Michelle E Martinez-Fernandez de la Camara, Cristina Bellingrath, Julia-Sophia Dauletbekov, Daniyar Ramsden, Simon C Hickey, Doron G Barnard, Alun R MacLaren, Robert E Producer: 20180423 In: Molecular therapy : the journal of the American Society of Gene Therapy vol. 25 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	18.	Genome-wide linkage and haplotype sharing analysis implicates the MCDR3 locus as a candidate region for a developmental macular disorder in association with digit abnormalities. [electronic resource] by Cipriani, Valentina Kalhoro, Ambreen Arno, Gavin Silva, Raquel S Pontikos, Nikolas Puech, Virginie McClements, Michelle E Hunt, David M van Heyningen, Veronica Michaelides, Michel Webster, Andrew R Moore, Anthony T Puech, Bernard Producer: 20171201 In: Ophthalmic genetics vol. 38 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	19.	Extended extraocular phenotype of PROM1 mutation in kindreds with known autosomal dominant macular dystrophy. [electronic resource] by Arrigoni, Francesca I Matarin, Mar Thompson, Pamela J Michaelides, Michel McClements, Michelle E Redmond, Elizabeth Clarke, Lindsey Ellins, Elizabeth Mohamed, Saifullah Pavord, Ian Klein, Nigel Hunt, David M Moore, Anthony T Halcox, Julian Sisodiya, Sanjay M Producer: 20110504 In: European journal of human genetics : EJHG vol. 19 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	20.	Long-term restoration of visual function in end-stage retinal degeneration using subretinal human melanopsin gene therapy. [electronic resource] by De Silva, Samantha R Barnard, Alun R Hughes, Steven Tam, Shu K E Martin, Chris Singh, Mandeep S Barnea-Cramer, Alona O McClements, Michelle E During, Matthew J Peirson, Stuart N Hankins, Mark W MacLaren, Robert E Producer: 20180618 In: Proceedings of the National Academy of Sciences of the United States of America vol. 114 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)

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Your search returned 20 results.