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Repeated aerosolized AAV-CFTR for treatment of cystic fibrosis: a randomized placebo-controlled phase 2B trial. [electronic resource] by
- Moss, Richard B
- Milla, Carlos
- Colombo, John
- Accurso, Frank
- Zeitlin, Pamela L
- Clancy, John P
- Spencer, L Terry
- Pilewski, Joseph
- Waltz, David A
- Dorkin, Henry L
- Ferkol, Thomas
- Pian, Mark
- Ramsey, Bonnie
- Carter, Barrie J
- Martin, Dana B
- Heald, Alison E
Producer: 20071011
In:
Human gene therapy vol. 18
Availability: No items available.
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10.
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Duchenne Regulatory Science Consortium Meeting on Disease Progression Modeling for Duchenne Muscular Dystrophy. [electronic resource] by
- Larkindale, Jane
- Abresch, Richard
- Aviles, Enrique
- Bronson, Abby
- Chin, Janice
- Furlong, Pat
- Gordish-Dressman, Heather
- Habeeb-Louks, Elizabeth
- Henricson, Erik
- Kroger, Hans
- Lynn, Charles
- Lynn, Stephen
- Martin, Dana
- Nuckolls, Glen
- Rooney, William
- Romero, Klaus
- Sweeney, Lee
- Vandenborne, Krista
- Walter, Glenn
- Wolff, Jodi
- Wong, Brenda
- McDonald, Craig M
- Duchenne Regulatory Science Consortium Imaging-Dmd Consortium And The Cinrg Investigators, Members Of The
Publication details: PLoS currents Jan 2017
In:
PLoS currents vol. 9
Availability: No items available.
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