Results
|
1.
|
|
|
2.
|
|
|
3.
|
|
|
4.
|
|
|
5.
|
|
|
6.
|
|
|
7.
|
|
|
8.
|
|
|
9.
|
|
|
10.
|
|
|
11.
|
|
|
12.
|
|
|
13.
|
Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs. [electronic resource] by
- Ye, Guo-Jie
- Komáromy, András M
- Zeiss, Caroline
- Calcedo, Roberto
- Harman, Christine D
- Koehl, Kristin L
- Stewart, Gabriel A
- Iwabe, Simone
- Chiodo, Vince A
- Hauswirth, William W
- Aguirre, Gustavo D
- Chulay, Jeffrey D
Producer: 20180730
In:
Human gene therapy. Clinical development vol. 28
Availability: No items available.
|
|
14.
|
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement. [electronic resource] by
- Cideciyan, Artur V
- Jacobson, Samuel G
- Beltran, William A
- Sumaroka, Alexander
- Swider, Malgorzata
- Iwabe, Simone
- Roman, Alejandro J
- Olivares, Melani B
- Schwartz, Sharon B
- Komáromy, András M
- Hauswirth, William W
- Aguirre, Gustavo D
Producer: 20130409
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 110
Availability: No items available.
|
|
15.
|
Canine retina has a primate fovea-like bouquet of cone photoreceptors which is affected by inherited macular degenerations. [electronic resource] by
- Beltran, William A
- Cideciyan, Artur V
- Guziewicz, Karina E
- Iwabe, Simone
- Swider, Malgorzata
- Scott, Erin M
- Savina, Svetlana V
- Ruthel, Gordon
- Stefano, Frank
- Zhang, Lingli
- Zorger, Richard
- Sumaroka, Alexander
- Jacobson, Samuel G
- Aguirre, Gustavo D
Producer: 20150113
In:
PloS one vol. 9
Availability: No items available.
|
|
16.
|
Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector. [electronic resource] by
- Cideciyan, Artur V
- Sudharsan, Raghavi
- Dufour, Valérie L
- Massengill, Michael T
- Iwabe, Simone
- Swider, Malgorzata
- Lisi, Brianna
- Sumaroka, Alexander
- Marinho, Luis Felipe
- Appelbaum, Tatyana
- Rossmiller, Brian
- Hauswirth, William W
- Jacobson, Samuel G
- Lewin, Alfred S
- Aguirre, Gustavo D
- Beltran, William A
Producer: 20181005
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 115
Availability: No items available.
|
|
17.
|
Overlap of abnormal photoreceptor development and progressive degeneration in Leber congenital amaurosis caused by NPHP5 mutation. [electronic resource] by
- Downs, Louise M
- Scott, Erin M
- Cideciyan, Artur V
- Iwabe, Simone
- Dufour, Valerie
- Gardiner, Kristin L
- Genini, Sem
- Marinho, Luis Felipe
- Sumaroka, Alexander
- Kosyk, Mychajlo S
- Swider, Malgorzata
- Aguirre, Geoffrey K
- Jacobson, Samuel G
- Beltran, William A
- Aguirre, Gustavo D
Producer: 20170609
In:
Human molecular genetics vol. 25
Availability: No items available.
|
|
18.
|
Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease. [electronic resource] by
- Beltran, William A
- Cideciyan, Artur V
- Iwabe, Simone
- Swider, Malgorzata
- Kosyk, Mychajlo S
- McDaid, Kendra
- Martynyuk, Inna
- Ying, Gui-Shuang
- Shaffer, James
- Deng, Wen-Tao
- Boye, Sanford L
- Lewin, Alfred S
- Hauswirth, William W
- Jacobson, Samuel G
- Aguirre, Gustavo D
Producer: 20160226
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 112
Availability: No items available.
|
|
19.
|
None [electronic resource] by
- Guziewicz, Karina E
- Cideciyan, Artur V
- Beltran, William A
- Komáromy, András M
- Dufour, Valerie L
- Swider, Malgorzata
- Iwabe, Simone
- Sumaroka, Alexander
- Kendrick, Brian T
- Ruthel, Gordon
- Chiodo, Vince A
- Héon, Elise
- Hauswirth, William W
- Jacobson, Samuel G
- Aguirre, Gustavo D
Producer: 20180918
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 115
Availability: No items available.
|
|
20.
|
Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa. [electronic resource] by
- Beltran, William A
- Cideciyan, Artur V
- Lewin, Alfred S
- Iwabe, Simone
- Khanna, Hemant
- Sumaroka, Alexander
- Chiodo, Vince A
- Fajardo, Diego S
- Román, Alejandro J
- Deng, Wen-Tao
- Swider, Malgorzata
- Alemán, Tomas S
- Boye, Sanford L
- Genini, Sem
- Swaroop, Anand
- Hauswirth, William W
- Jacobson, Samuel G
- Aguirre, Gustavo D
Producer: 20120330
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 109
Availability: No items available.
|