Results
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1.
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A Phase I/IIa Safety and Efficacy Study of Nebulized Liposome-mediated Gene Therapy for Cystic Fibrosis Supports a Multidose Trial. [electronic resource] by
- Alton, Eric W F W
- Boyd, A Christopher
- Porteous, David J
- Davies, Gwyneth
- Davies, Jane C
- Griesenbach, Uta
- Higgins, Tracy E
- Gill, Deborah R
- Hyde, Stephen C
- Innes, J Alastair
Producer: 20160404
In:
American journal of respiratory and critical care medicine vol. 192
Availability: No items available.
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2.
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Self-reactive CFTR T cells in humans: implications for gene therapy. [electronic resource] by
- Calcedo, Roberto
- Griesenbach, Uta
- Dorgan, Daniel J
- Soussi, Samia
- Boyd, A Christopher
- Davies, Jane C
- Higgins, Tracy E
- Hyde, Stephen C
- Gill, Deborah R
- Innes, J Alastair
- Porteous, David J
- Alton, Eric W
- Wilson, James M
- Limberis, Maria P
Producer: 20140501
In:
Human gene therapy. Clinical development vol. 24
Availability: No items available.
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3.
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Assessment of F/HN-pseudotyped lentivirus as a clinically relevant vector for lung gene therapy. [electronic resource] by
- Griesenbach, Uta
- Inoue, Makoto
- Meng, Cuixiang
- Farley, Raymond
- Chan, Mario
- Newman, Nikki K
- Brum, Andrea
- You, Jun
- Kerton, Angela
- Shoemark, Amelia
- Boyd, A Christopher
- Davies, Jane C
- Higgins, Tracy E
- Gill, Deborah R
- Hyde, Stephen C
- Innes, J Alastair
- Porteous, David J
- Hasegawa, Mamoru
- Alton, Eric W F W
Producer: 20130108
In:
American journal of respiratory and critical care medicine vol. 186
Availability: No items available.
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4.
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Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis. [electronic resource] by
- Alton, Eric W F W
- Beekman, Jeffery M
- Boyd, A Christopher
- Brand, June
- Carlon, Marianne S
- Connolly, Mary M
- Chan, Mario
- Conlon, Sinead
- Davidson, Heather E
- Davies, Jane C
- Davies, Lee A
- Dekkers, Johanna F
- Doherty, Ann
- Gea-Sorli, Sabrina
- Gill, Deborah R
- Griesenbach, Uta
- Hasegawa, Mamoru
- Higgins, Tracy E
- Hironaka, Takashi
- Hyndman, Laura
- McLachlan, Gerry
- Inoue, Makoto
- Hyde, Stephen C
- Innes, J Alastair
- Maher, Toby M
- Moran, Caroline
- Meng, Cuixiang
- Paul-Smith, Michael C
- Pringle, Ian A
- Pytel, Kamila M
- Rodriguez-Martinez, Andrea
- Schmidt, Alexander C
- Stevenson, Barbara J
- Sumner-Jones, Stephanie G
- Toshner, Richard
- Tsugumine, Shu
- Wasowicz, Marguerite W
- Zhu, Jie
Producer: 20170615
In:
Thorax vol. 72
Availability: No items available.
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5.
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Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial. [electronic resource] by
- Alton, Eric W F W
- Armstrong, David K
- Ashby, Deborah
- Bayfield, Katie J
- Bilton, Diana
- Bloomfield, Emily V
- Boyd, A Christopher
- Brand, June
- Buchan, Ruaridh
- Calcedo, Roberto
- Carvelli, Paula
- Chan, Mario
- Cheng, Seng H
- Collie, D David S
- Cunningham, Steve
- Davidson, Heather E
- Davies, Gwyneth
- Davies, Jane C
- Davies, Lee A
- Dewar, Maria H
- Doherty, Ann
- Donovan, Jackie
- Dwyer, Natalie S
- Elgmati, Hala I
- Featherstone, Rosanna F
- Gavino, Jemyr
- Gea-Sorli, Sabrina
- Geddes, Duncan M
- Gibson, James S R
- Gill, Deborah R
- Greening, Andrew P
- Griesenbach, Uta
- Hansell, David M
- Harman, Katharine
- Higgins, Tracy E
- Hodges, Samantha L
- Hyde, Stephen C
- Hyndman, Laura
- Innes, J Alastair
- Jacob, Joseph
- Jones, Nancy
- Keogh, Brian F
- Limberis, Maria P
- Lloyd-Evans, Paul
- Maclean, Alan W
- Manvell, Michelle C
- McCormick, Dominique
- McGovern, Michael
- McLachlan, Gerry
- Meng, Cuixiang
- Montero, M Angeles
- Milligan, Hazel
- Moyce, Laura J
- Murray, Gordon D
- Nicholson, Andrew G
- Osadolor, Tina
- Parra-Leiton, Javier
- Porteous, David J
- Pringle, Ian A
- Punch, Emma K
- Pytel, Kamila M
- Quittner, Alexandra L
- Rivellini, Gina
- Saunders, Clare J
- Scheule, Ronald K
- Sheard, Sarah
- Simmonds, Nicholas J
- Smith, Keith
- Smith, Stephen N
- Soussi, Najwa
- Soussi, Samia
- Spearing, Emma J
- Stevenson, Barbara J
- Sumner-Jones, Stephanie G
- Turkkila, Minna
- Ureta, Rosa P
- Waller, Michael D
- Wasowicz, Marguerite Y
- Wilson, James M
- Wolstenholme-Hogg, Paul
Producer: 20160720
In:
The Lancet. Respiratory medicine vol. 3
Availability: No items available.
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