Glia-to-Neuron Conversion by CRISPR-CasRx Alleviates Symptoms of Neurological Disease in Mice. [electronic resource]
Producer: 20210104Description: 590-603.e16 p. digitalISSN:- 1097-4172
- Animals
- CRISPR-Cas Systems -- physiology
- Cell Differentiation -- physiology
- Cells, Cultured
- Clustered Regularly Interspaced Short Palindromic Repeats -- genetics
- Disease Models, Animal
- Dopamine -- metabolism
- Gene Expression Regulation -- genetics
- Heterogeneous-Nuclear Ribonucleoproteins -- genetics
- Male
- Mice
- Mice, Inbred C57BL
- Nervous System Diseases -- metabolism
- Neurogenesis -- physiology
- Neuroglia -- metabolism
- Neurons -- metabolism
- Parkinson Disease -- metabolism
- Polypyrimidine Tract-Binding Protein -- genetics
- Retinal Ganglion Cells -- metabolism
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Publication Type: Journal Article; Research Support, Non-U.S. Gov't
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