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European Cross-Sectional Survey of Current Care Practices for Duchenne Muscular Dystrophy Reveals Regional and Age-Dependent Differences. [electronic resource] by
- Vry, Julia
- Gramsch, Kathrin
- Rodger, Sunil
- Thompson, Rachel
- Steffensen, Birgit F
- Rahbek, Jes
- Doerken, Sam
- Tassoni, Adrian
- Beytía, María de Los Angeles
- Guergueltcheva, Velina
- Chamova, Teodora
- Tournev, Ivailo
- Kostera-Pruszczyk, Anna
- Kaminska, Anna
- Lusakowska, Anna
- Mrazova, Lenka
- Pavlovska, Lenka
- Strenkova, Jana
- Vondráček, Petr
- Garami, Marta
- Karcagi, Veronika
- Herczegfalvi, Ágnes
- Bushby, Katherine
- Lochmüller, Hanns
- Kirschner, Janbernd
Producer: 20180315
In:
Journal of neuromuscular diseases vol. 3
Availability: No items available.
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A prospective study on the natural history of patients with profound combined immunodeficiency: An interim analysis. [electronic resource] by
- Speckmann, Carsten
- Doerken, Sam
- Aiuti, Alessandro
- Albert, Michael H
- Al-Herz, Waleed
- Allende, Luis M
- Scarselli, Alessia
- Avcin, Tadej
- Perez-Becker, Ruy
- Cancrini, Caterina
- Cant, Andrew
- Di Cesare, Silvia
- Finocchi, Andrea
- Fischer, Alain
- Gaspar, H Bobby
- Ghosh, Sujal
- Gennery, Andrew
- Gilmour, Kimberly
- González-Granado, Luis I
- Martinez-Gallo, Monica
- Hambleton, Sophie
- Hauck, Fabian
- Hoenig, Manfred
- Moshous, Despina
- Neven, Benedicte
- Niehues, Tim
- Notarangelo, Luigi
- Picard, Capucine
- Rieber, Nikolaus
- Schulz, Ansgar
- Schwarz, Klaus
- Seidel, Markus G
- Soler-Palacin, Pere
- Stepensky, Polina
- Strahm, Brigitte
- Vraetz, Thomas
- Warnatz, Klaus
- Winterhalter, Christine
- Worth, Austen
- Fuchs, Sebastian
- Uhlmann, Annette
- Ehl, Stephan
Producer: 20170724
In:
The Journal of allergy and clinical immunology vol. 139
Availability: No items available.
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