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	1.	An online survey of burden of illness in families with mucopolysaccharidosis type II children in the United States. [electronic resource] by Conner, Therese Cook, Francesca Fernandez, Vivian Rangel-Miller, Vanessa Publication details: Molecular genetics and metabolism reports Dec 2019 In: Molecular genetics and metabolism reports vol. 21 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	2.	An online survey on burden of illness among families with post-stem cell transplant mucopolysaccharidosis type I children in the United States. [electronic resource] by Conner, Therese Cook, Francesca Fernandez, Vivian Rascati, Karen Rangel-Miller, Vanessa Producer: 20190419 In: Orphanet journal of rare diseases vol. 14 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	3.	Addressing the Value of Gene Therapy and Enhancing Patient Access to Transformative Treatments. [electronic resource] by Salzman, Rachel Cook, Francesca Hunt, Timothy Malech, Harry L Reilly, Philip Foss-Campbell, Betsy Barrett, David Producer: 20190930 In: Molecular therapy : the journal of the American Society of Gene Therapy vol. 26 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)

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