Clinical utility of neuronal cells directly converted from fibroblasts of patients for neuropsychiatric disorders: studies of lysosomal storage diseases and channelopathy. [electronic resource]
Producer: 20151218Description: 138-45 p. digitalISSN:- 1875-5666
- 1-Deoxynojirimycin -- analogs & derivatives
- Action Potentials -- drug effects
- Basic Helix-Loop-Helix Transcription Factors -- genetics
- Cell Differentiation
- Epilepsies, Myoclonic -- metabolism
- Fibroblasts -- drug effects
- G(M2) Ganglioside -- metabolism
- Gene Expression
- Genetic Vectors -- chemistry
- Glycoside Hydrolase Inhibitors -- pharmacology
- Humans
- Lentivirus -- genetics
- Nerve Tissue Proteins -- genetics
- Neurons -- drug effects
- Plasmids -- chemistry
- Primary Cell Culture
- Tay-Sachs Disease -- metabolism
- Transcription Factors -- genetics
- Transduction, Genetic
- Transgenes
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Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
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