Adenovirus expressing an NPC1-GFP fusion gene corrects neuronal and nonneuronal defects associated with Niemann pick type C disease. [electronic resource]
Producer: 20051101Description: 706-19 p. digitalISSN:- 0360-4012
- Adenoviridae -- genetics
- Animals
- Astrocytes -- metabolism
- Biological Transport -- physiology
- Brain -- metabolism
- CHO Cells
- Carrier Proteins -- metabolism
- Cholesterol -- metabolism
- Cricetinae
- Female
- Fibroblasts -- metabolism
- Genetic Techniques
- Green Fluorescent Proteins -- metabolism
- Humans
- Intracellular Signaling Peptides and Proteins
- Membrane Glycoproteins -- metabolism
- Mice
- Microscopy, Fluorescence
- Neurons -- metabolism
- Niemann-Pick C1 Protein
- Niemann-Pick Diseases -- genetics
- Ovary -- cytology
- Rats
- Recombinant Fusion Proteins
- Transduction, Genetic
- Transfection
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Publication Type: Comparative Study; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
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