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Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy. [electronic resource] by
- Long, Chengzu
- Amoasii, Leonela
- Mireault, Alex A
- McAnally, John R
- Li, Hui
- Sanchez-Ortiz, Efrain
- Bhattacharyya, Samadrita
- Shelton, John M
- Bassel-Duby, Rhonda
- Olson, Eric N
Producer: 20160204
In:
Science (New York, N.Y.) vol. 351
Availability: No items available.
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In vivo non-invasive monitoring of dystrophin correction in a new Duchenne muscular dystrophy reporter mouse. [electronic resource] by
- Amoasii, Leonela
- Li, Hui
- Zhang, Yu
- Min, Yi-Li
- Sanchez-Ortiz, Efrain
- Shelton, John M
- Long, Chengzu
- Mireault, Alex A
- Bhattacharyya, Samadrita
- McAnally, John R
- Bassel-Duby, Rhonda
- Olson, Eric N
Producer: 20200214
In:
Nature communications vol. 10
Availability: No items available.
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8.
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Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy. [electronic resource] by
- Amoasii, Leonela
- Long, Chengzu
- Li, Hui
- Mireault, Alex A
- Shelton, John M
- Sanchez-Ortiz, Efrain
- McAnally, John R
- Bhattacharyya, Samadrita
- Schmidt, Florian
- Grimm, Dirk
- Hauschka, Stephen D
- Bassel-Duby, Rhonda
- Olson, Eric N
Producer: 20180717
In:
Science translational medicine vol. 9
Availability: No items available.
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