Results
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801.
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802.
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803.
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804.
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Efficacy of enzyme replacement therapy in alpha-mannosidosis mice: a preclinical animal study. [electronic resource] by
- Roces, Diego Prieto
- Lüllmann-Rauch, Renate
- Peng, Jianhe
- Balducci, Chiara
- Andersson, Claes
- Tollersrud, Ole
- Fogh, Jens
- Orlacchio, Aldo
- Beccari, Tommaso
- Saftig, Paul
- von Figura, Kurt
Producer: 20050315
In:
Human molecular genetics vol. 13
Availability: No items available.
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805.
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806.
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807.
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808.
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809.
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810.
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811.
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Mannosidase 2, alpha 1 deficiency is associated with ricin resistance in embryonic stem (ES) cells. [electronic resource] by
- Wang, Wei
- Hale, Christine
- Goulding, Dave
- Haslam, Stuart M
- Tissot, Bérangère
- Lindsay, Christopher
- Michell, Stephen
- Titball, Rick
- Yu, Jun
- Toribio, Ana Luisa
- Rossi, Raffaella
- Dell, Anne
- Bradley, Allan
- Dougan, Gordon
Producer: 20120111
In:
PloS one vol. 6
Availability: No items available.
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812.
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MANBA, CXCR5, SOX8, RPS6KB1 and ZBTB46 are genetic risk loci for multiple sclerosis. [electronic resource] by
- Lill, Christina M
- Schjeide, Brit-Maren M
- Graetz, Christine
- Ban, Maria
- Alcina, Antonio
- Ortiz, Miguel A
- Pérez, Jennifer
- Damotte, Vincent
- Booth, David
- Lopez de Lapuente, Aitzkoa
- Broer, Linda
- Schilling, Marcel
- Akkad, Denis A
- Aktas, Orhan
- Alloza, Iraide
- Antigüedad, Alfredo
- Arroyo, Rafa
- Blaschke, Paul
- Buttmann, Mathias
- Chan, Andrew
- Compston, Alastair
- Cournu-Rebeix, Isabelle
- Dörner, Thomas
- Epplen, Joerg T
- Fernández, Óscar
- Gerdes, Lisa-Ann
- Guillot-Noël, Léna
- Hartung, Hans-Peter
- Hoffjan, Sabine
- Izquierdo, Guillermo
- Kemppinen, Anu
- Kroner, Antje
- Kubisch, Christian
- Kümpfel, Tania
- Li, Shu-Chen
- Lindenberger, Ulman
- Lohse, Peter
- Lubetzki, Catherine
- Luessi, Felix
- Malhotra, Sunny
- Mescheriakova, Julia
- Montalban, Xavier
- Papeix, Caroline
- Paredes, Lidia F
- Rieckmann, Peter
- Steinhagen-Thiessen, Elisabeth
- Winkelmann, Alexander
- Zettl, Uwe K
- Hintzen, Rogier
- Vandenbroeck, Koen
- Stewart, Graeme
- Fontaine, Bertrand
- Comabella, Manuel
- Urcelay, Elena
- Matesanz, Fuencisla
- Sawcer, Stephen
- Bertram, Lars
- Zipp, Frauke
Producer: 20130807
In:
Brain : a journal of neurology vol. 136
Availability: No items available.
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813.
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814.
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815.
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816.
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817.
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818.
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819.
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820.
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Comprehensive long-term efficacy and safety of recombinant human alpha-mannosidase (velmanase alfa) treatment in patients with alpha-mannosidosis. [electronic resource] by
- Lund, Allan M
- Borgwardt, Line
- Cattaneo, Federica
- Ardigò, Diego
- Geraci, Silvia
- Gil-Campos, Mercedes
- De Meirleir, Linda
- Laroche, Cécile
- Dolhem, Philippe
- Cole, Duncan
- Tylki-Szymanska, Anna
- Lopez-Rodriguez, Monica
- Guillén-Navarro, Encarna
- Dali, Christine I
- Héron, Bénédicte
- Fogh, Jens
- Muschol, Nicole
- Phillips, Dawn
- Van den Hout, J M Hannerieke
- Jones, Simon A
- Amraoui, Yasmina
- Harmatz, Paul
- Guffon, Nathalie
Producer: 20191104
In:
Journal of inherited metabolic disease vol. 41
Availability: No items available.
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