Results
|
7821.
|
|
|
7822.
|
AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort. [electronic resource] by
- Al-Zaidy, Samiah A
- Kolb, Stephen J
- Lowes, Linda
- Alfano, Lindsay N
- Shell, Richard
- Church, Kathleen R
- Nagendran, Sukumar
- Sproule, Douglas M
- Feltner, Douglas E
- Wells, Courtney
- Ogrinc, Francis
- Menier, Melissa
- L'Italien, James
- Arnold, W David
- Kissel, John T
- Kaspar, Brian K
- Mendell, Jerry R
Producer: 20200217
In:
Journal of neuromuscular diseases vol. 6
Availability: No items available.
|
|
7823.
|
|
|
7824.
|
Nonalcoholic fatty liver disease in patients with inflammatory bowel disease: Beyond the natural history. [electronic resource] by
- Magrì, Salvatore
- Paduano, Danilo
- Chicco, Fabio
- Cingolani, Arianna
- Farris, Cristiana
- Delogu, Giovanna
- Tumbarello, Francesca
- Lai, Mariantonia
- Melis, Alessandro
- Casula, Laura
- Fantini, Massimo C
- Usai, Paolo
Producer: 20200226
In:
World journal of gastroenterology vol. 25
Availability: No items available.
|
|
7825.
|
Pycnodysostosis: Natural history and management guidelines from 27 French cases and a literature review. [electronic resource] by
- Bizaoui, Varoona
- Michot, Caroline
- Baujat, Geneviève
- Amouroux, Cyril
- Baron, Sabine
- Capri, Yline
- Cohen-Solal, Martine
- Collet, Corinne
- Dieux, Anne
- Geneviève, David
- Isidor, Bertrand
- Monnot, Sophie
- Rossi, Massimiliano
- Rothenbuhler, Anya
- Schaefer, Elise
- Cormier-Daire, Valérie
Producer: 20200903
In:
Clinical genetics vol. 96
Availability: No items available.
|
|
7826.
|
|
|
7827.
|
Differences in cardiac phenotype and natural history of laminopathies with and without neuromuscular onset. [electronic resource] by
- Ditaranto, Raffaello
- Boriani, Giuseppe
- Biffi, Mauro
- Lorenzini, Massimiliano
- Graziosi, Maddalena
- Ziacchi, Matteo
- Pasquale, Ferdinando
- Vitale, Giovanni
- Berardini, Alessandra
- Rinaldi, Rita
- Lattanzi, Giovanna
- Potena, Luciano
- Martin Suarez, Sofia
- Bacchi Reggiani, Maria Letizia
- Rapezzi, Claudio
- Biagini, Elena
Producer: 20200724
In:
Orphanet journal of rare diseases vol. 14
Availability: No items available.
|
|
7828.
|
|
|
7829.
|
|
|
7830.
|
|
|
7831.
|
|
|
7832.
|
|
|
7833.
|
|
|
7834.
|
|
|
7835.
|
|
|
7836.
|
|
|
7837.
|
|
|
7838.
|
|
|
7839.
|
|
|
7840.
|
|