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722.
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Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy. [electronic resource] by
- Gentner, Bernhard
- Visigalli, Ilaria
- Hiramatsu, Hidefumi
- Lechman, Eric
- Ungari, Silvia
- Giustacchini, Alice
- Schira, Giulia
- Amendola, Mario
- Quattrini, Angelo
- Martino, Sabata
- Orlacchio, Aldo
- Dick, John E
- Biffi, Alessandra
- Naldini, Luigi
Producer: 20110610
In:
Science translational medicine vol. 2
Availability: No items available.
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725.
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728.
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729.
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730.
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732.
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735.
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736.
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737.
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738.
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739.
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740.
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