Results
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641.
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Glycoengineered acid alpha-glucosidase with improved efficacy at correcting the metabolic aberrations and motor function deficits in a mouse model of Pompe disease. [electronic resource] by
- Zhu, Yunxiang
- Jiang, Ji-Lei
- Gumlaw, Nathan K
- Zhang, Jinhua
- Bercury, Scott D
- Ziegler, Robin J
- Lee, Karen
- Kudo, Mariko
- Canfield, William M
- Edmunds, Timothy
- Jiang, Canwen
- Mattaliano, Robert J
- Cheng, Seng H
Producer: 20090807
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 17
Availability: No items available.
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642.
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643.
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644.
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645.
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646.
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Bicistronic lentiviral vector corrects beta-hexosaminidase deficiency in transduced and cross-corrected human Sandhoff fibroblasts. [electronic resource] by
- Arfi, Audrey
- Bourgoin, Christophe
- Basso, Luisa
- Emiliani, Carla
- Tancini, Brunella
- Chigorno, Vanna
- Li, Yu-Teh
- Orlacchio, Aldo
- Poenaru, Livia
- Sonnino, Sandro
- Caillaud, Catherine
Producer: 20060123
In:
Neurobiology of disease vol. 20
Availability: No items available.
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647.
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648.
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