Results
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Intrathecal heparan-N-sulfatase in patients with Sanfilippo syndrome type A: A phase IIb randomized trial. [electronic resource] by
- Wijburg, Frits A
- Whitley, Chester B
- Muenzer, Joseph
- Gasperini, Serena
- Del Toro, Mireia
- Muschol, Nicole
- Cleary, Maureen
- Sevin, Caroline
- Shapiro, Elsa
- Bhargava, Parul
- Kerr, Douglas
- Alexanderian, David
Producer: 20190808
In:
Molecular genetics and metabolism vol. 126
Availability: No items available.
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