Your search returned 635 results.

Results
	61.	Molecular biology. A splicing magic bullet. [electronic resource] by Vigevani, Luisa Valcárcel, Juan Producer: 20140826 In: Science (New York, N.Y.) vol. 345 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	62.	Nusinersen: The First Option Beyond Supportive Care for Spinal Muscular Atrophy. [electronic resource] by Maharshi, Vikas Hasan, Shazia Producer: 20180528 In: Clinical drug investigation vol. 37 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	63.	Splicing of the Survival Motor Neuron genes and implications for treatment of SMA [electronic resource] by Bebee, Thomas W Gladman, Jordan T Chandler, Dawn S Producer: 20100916 In: Frontiers in bioscience (Landmark edition) vol. 15 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	64.	Spinal muscular atrophy and the antiapoptotic role of survival of motor neuron (SMN) protein. [electronic resource] by Anderton, Ryan S Meloni, Bruno P Mastaglia, Frank L Boulos, Sherif Producer: 20140213 In: Molecular neurobiology vol. 47 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	65.	Therapeutics that directly increase SMN expression to treat spinal muscular atrophy. [electronic resource] by Shababi, Monir Mattis, Virginia B Lorson, Christian L Producer: 20110224 In: Drug news & perspectives vol. 23 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	66.	Targeting RNA-splicing for SMA treatment. [electronic resource] by Zhou, Jianhua Zheng, Xuexiu Shen, Haihong Producer: 20120713 In: Molecules and cells vol. 33 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	67.	Sense in antisense therapy for spinal muscular atrophy. [electronic resource] by MacKenzie, Alex Producer: 20120228 In: The New England journal of medicine vol. 366 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	68.	Neuromuscular disorders: Beefing up the right splice variant to treat spinal muscular atrophy. [electronic resource] by Cully, Megan Producer: 20141201 In: Nature reviews. Drug discovery vol. 13 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	69.	Universal fluorescent tri-probe ligation equipped with capillary electrophoresis for targeting SMN1 and SMN2 genes in diagnosis of spinal muscular atrophy. [electronic resource] by Wang, Chun-Chi Shih, Chi-Jen Jong, Yuh-Jyh Wu, Shou-Mei Producer: 20150420 In: Analytica chimica acta vol. 833 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	70.	Splicing solutions: Companies explore new techniques to fix splicing errors. [electronic resource] by Chakradhar, Shraddha Producer: 20180130 In: Nature medicine vol. 22 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	71.	Rescue of a severe mouse model for spinal muscular atrophy by U7 snRNA-mediated splicing modulation. [electronic resource] by Meyer, Kathrin Marquis, Julien Trüb, Judith Nlend Nlend, Rachel Verp, Sonia Ruepp, Marc-David Imboden, Hans Barde, Isabelle Trono, Didier Schümperli, Daniel Producer: 20090227 In: Human molecular genetics vol. 18 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	72.	Spinal Muscular Atrophy and Common Therapeutic Advances. [electronic resource] by Bozorg Qomi, Saeed Asghari, Amir Salmaninejad, Arash Mojarrad, Majid Producer: 20191212 In: Fetal and pediatric pathology vol. 38 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	73.	Activation of the intronic cryptic 5' splice site depends on its distance to the upstream cassette exon. [electronic resource] by Liu, Wei Li, Xia Liao, Shengjie Dou, Kefeng Zhang, Yi Producer: 20170608 In: Gene vol. 619 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	74.	Augmenting the SMN Protein to Treat Infantile Spinal Muscular Atrophy. [electronic resource] by Kim, Jeong-Ki Monani, Umrao R Producer: 20190715 In: Neuron vol. 97 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	75.	Homozygous SMN2 deletion is a protective factor in the Swedish ALS population. [electronic resource] by Corcia, Philippe Ingre, Caroline Blasco, Helene Press, Rayomand Praline, Julien Antar, Catherine Veyrat-Durebex, Charlotte Guettard, Yves-Olivier Camu, William Andersen, Peter M Vourc'h, Patrick Andres, Christian R Producer: 20120910 In: European journal of human genetics : EJHG vol. 20 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	76.	TSUNAMI: an antisense method to phenocopy splicing-associated diseases in animals. [electronic resource] by Sahashi, Kentaro Hua, Yimin Ling, Karen K Y Hung, Gene Rigo, Frank Horev, Guy Katsuno, Masahisa Sobue, Gen Ko, Chien-Ping Bennett, C Frank Krainer, Adrian R Producer: 20121029 In: Genes & development vol. 26 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	77.	Spinal muscular atrophy due to double gene conversion event. [electronic resource] by Maamouri, Wiéme Hammer, Monia Benhamed Bouhlel, Yosr Souilem, Sihem Khmiri, Najla Nehdi, Houda Hentati, Fayçal Amouri, Rim Producer: 20110503 In: The International journal of neuroscience vol. 121 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	78.	Molecular therapeutic strategies for spinal muscular atrophies: current and future clinical trials. [electronic resource] by Zanetta, Chiara Nizzardo, Monica Simone, Chiara Monguzzi, Erika Bresolin, Nereo Comi, Giacomo P Corti, Stefania Producer: 20141104 In: Clinical therapeutics vol. 36 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	79.	Two breakthrough gene-targeted treatments for spinal muscular atrophy: challenges remain. [electronic resource] by Sumner, Charlotte J Crawford, Thomas O Producer: 20190910 In: The Journal of clinical investigation vol. 128 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	80.	Splicing therapeutics in SMN2 and APOB. [electronic resource] by Khoo, Bernard Krainer, Adrian R Producer: 20090611 In: Current opinion in molecular therapeutics vol. 11 Availability: No items available. Save to lists Add to cart (remove)

First
Previous
1
2
3
4
5
6
7
8
9
10
Next
Last

Refine your search

Availability

Authors

Topics

Languages

Your search returned 635 results.