Results
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5921.
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5922.
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ESCRT-mediated uptake and degradation of brain-targeted α-synuclein single chain antibody attenuates neuronal degeneration in vivo. [electronic resource] by
- Spencer, Brian
- Emadi, Sharareh
- Desplats, Paula
- Eleuteri, Simona
- Michael, Sarah
- Kosberg, Kori
- Shen, Jay
- Rockenstein, Edward
- Patrick, Christina
- Adame, Anthony
- Gonzalez, Tania
- Sierks, Michael
- Masliah, Eliezer
Producer: 20150610
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 22
Availability: No items available.
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5923.
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5924.
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α- L-iduronidase gene-based therapy using the phiC31 system to treat mucopolysaccharidose type I mice. [electronic resource] by
- Stilhano, Roberta Sessa
- Martin, Priscila Keiko Matsumoto
- de Melo, Suely Maymone
- Samoto, Vivian Yochiko
- Peres, Giovani Bravin
- da Silva Michelacci, Yara Maria Correa
- da Silva, Flavia Helena
- Pereira, Vanessa Gonçalves
- D'Almeida, Vania
- da Cruz, Adriana Taveira
- Jasiulionis, Miriam Galvonas
- Han, Sang Won
Producer: 20151217
In:
The journal of gene medicine vol. 17
Availability: No items available.
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5925.
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5926.
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Oncolytic Activity of a Novel Influenza A Virus Carrying Granulocyte-Macrophage Colony-Stimulating Factor in Hepatocellular Carcinoma. [electronic resource] by
- Penghui, Yang
- Fang, Sun
- Ruilan, Wang
- Guanglin, Lei
- Hongjing, Gu
- Yueqiang, Duan
- Zhongpeng, Zhao
- Xiaolan, Yang
- Zhaohai, Wang
- Shaogeng, Zhang
- Xiliang, Wang
Producer: 20200312
In:
Human gene therapy vol. 30
Availability: No items available.
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5927.
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Human chromosome 19 and related regions in mouse: conservative and lineage-specific evolution. [electronic resource] by
- Dehal, P
- Predki, P
- Olsen, A S
- Kobayashi, A
- Folta, P
- Lucas, S
- Land, M
- Terry, A
- Ecale Zhou, C L
- Rash, S
- Zhang, Q
- Gordon, L
- Kim, J
- Elkin, C
- Pollard, M J
- Richardson, P
- Rokhsar, D
- Uberbacher, E
- Hawkins, T
- Branscomb, E
- Stubbs, L
Producer: 20010719
In:
Science (New York, N.Y.) vol. 293
Availability: No items available.
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5928.
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5929.
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5930.
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5931.
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5932.
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5933.
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5934.
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5935.
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5936.
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5937.
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5938.
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A missense mutation in PIK3R5 gene in a family with ataxia and oculomotor apraxia. [electronic resource] by
- Al Tassan, Nada
- Khalil, Dania
- Shinwari, Jameela
- Al Sharif, Latifa
- Bavi, Prashant
- Abduljaleel, Zainularifeen
- Abu Dhaim, Nada
- Magrashi, Amna
- Bobis, Steve
- Ahmed, Hala
- Alahmed, Samaher
- Bohlega, Saeed
Producer: 20120514
In:
Human mutation vol. 33
Availability: No items available.
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5939.
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5940.
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