Results
|
|
41.
|
Long-term engraftment of single genetically modified human epidermal holoclones enables safety pre-assessment of cutaneous gene therapy. [electronic resource] by
- Larcher, Fernando
- Dellambra, Elena
- Rico, Laura
- Bondanza, Sergio
- Murillas, Rodolfo
- Cattoglio, Claudia
- Mavilio, Fulvio
- Jorcano, José L
- Zambruno, Giovanna
- Del Rio, Marcela
Producer: 20080226
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 15
Availability: No items available.
|
|
|
42.
|
Stem cell plasticity: time for a reappraisal? [electronic resource] by
- Lemoli, Roberto M
- Bertolini, Francesco
- Cancedda, Ranieri
- De Luca, Michele
- Del Santo, Antonio
- Ferrari, Giuliana
- Ferrari, Sergio
- Martino, Gianvito
- Mavilio, Fulvio
- Tura, Sante
Producer: 20060523
In:
Haematologica vol. 90
Availability: No items available.
|
|
|
43.
|
Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency. [electronic resource] by
- Poletti, Valentina
- Charrier, Sabine
- Corre, Guillaume
- Gjata, Bernard
- Vignaud, Alban
- Zhang, Fang
- Rothe, Michael
- Schambach, Axel
- Gaspar, H Bobby
- Thrasher, Adrian J
- Mavilio, Fulvio
Publication details: Molecular therapy. Methods & clinical development Jun 2018
In:
Molecular therapy. Methods & clinical development vol. 9
Availability: No items available.
|
|
|
44.
|
Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation. [electronic resource] by
- Cavazza, Alessia
- Miccio, Annarita
- Romano, Oriana
- Petiti, Luca
- Malagoli Tagliazucchi, Guidantonio
- Peano, Clelia
- Severgnini, Marco
- Rizzi, Ermanno
- De Bellis, Gianluca
- Bicciato, Silvio
- Mavilio, Fulvio
Producer: 20170111
In:
Stem cell reports vol. 6
Availability: No items available.
|
|
|
45.
|
Nuclear architecture dictates HIV-1 integration site selection. [electronic resource] by
- Marini, Bruna
- Kertesz-Farkas, Attila
- Ali, Hashim
- Lucic, Bojana
- Lisek, Kamil
- Manganaro, Lara
- Pongor, Sandor
- Luzzati, Roberto
- Recchia, Alessandra
- Mavilio, Fulvio
- Giacca, Mauro
- Lusic, Marina
Producer: 20150702
In:
Nature vol. 521
Availability: No items available.
|
|
|
46.
|
Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison Study. [electronic resource] by
- Urbinati, Fabrizia
- Campo Fernandez, Beatriz
- Masiuk, Katelyn E
- Poletti, Valentina
- Hollis, Roger P
- Koziol, Colin
- Kaufman, Michael L
- Brown, Devin
- Mavilio, Fulvio
- Kohn, Donald B
Producer: 20190819
In:
Human gene therapy vol. 29
Availability: No items available.
|
|
|
47.
|
Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell Disease. [electronic resource] by
- Poletti, Valentina
- Urbinati, Fabrizia
- Charrier, Sabine
- Corre, Guillaume
- Hollis, Roger P
- Campo Fernandez, Beatriz
- Martin, Samia
- Rothe, Michael
- Schambach, Axel
- Kohn, Donald B
- Mavilio, Fulvio
Publication details: Molecular therapy. Methods & clinical development Dec 2018
In:
Molecular therapy. Methods & clinical development vol. 11
Availability: No items available.
|
|
|
48.
|
High-definition mapping of retroviral integration sites identifies active regulatory elements in human multipotent hematopoietic progenitors. [electronic resource] by
- Cattoglio, Claudia
- Pellin, Danilo
- Rizzi, Ermanno
- Maruggi, Giulietta
- Corti, Giorgio
- Miselli, Francesca
- Sartori, Daniela
- Guffanti, Alessandro
- Di Serio, Clelia
- Ambrosi, Alessandro
- De Bellis, Gianluca
- Mavilio, Fulvio
Producer: 20110208
In:
Blood vol. 116
Availability: No items available.
|
|
|
49.
|
Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication. [electronic resource] by
- Di Nunzio, Francesca
- Fricke, Thomas
- Miccio, Annarita
- Valle-Casuso, Jose Carlos
- Perez, Patricio
- Souque, Philippe
- Rizzi, Ermanno
- Severgnini, Marco
- Mavilio, Fulvio
- Charneau, Pierre
- Diaz-Griffero, Felipe
Producer: 20130611
In:
Virology vol. 440
Availability: No items available.
|
|
|
50.
|
Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy. [electronic resource] by
- Armbruster, Nicole
- Lattanzi, Annalisa
- Jeavons, Matthieu
- Van Wittenberghe, Laetitia
- Gjata, Bernard
- Marais, Thibaut
- Martin, Samia
- Vignaud, Alban
- Voit, Thomas
- Mavilio, Fulvio
- Barkats, Martine
- Buj-Bello, Ana
Producer: 20160921
In:
Molecular therapy. Methods & clinical development vol. 3
Availability: No items available.
|
|
|
51.
|
Correction of laminin-5 deficiency in human epidermal stem cells by transcriptionally targeted lentiviral vectors. [electronic resource] by
- Di Nunzio, Francesca
- Maruggi, Giulietta
- Ferrari, Stefano
- Di Iorio, Enzo
- Poletti, Valentina
- Garcia, Marta
- Del Rio, Marcela
- De Luca, Michele
- Larcher, Fernando
- Pellegrini, Graziella
- Mavilio, Fulvio
Producer: 20090107
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 16
Availability: No items available.
|
|
|
52.
|
Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in non-human primates. [electronic resource] by
- Matet, Alexandre
- Kostic, Corinne
- Bemelmans, Alexis-Pierre
- Moulin, Alexandre
- Rosolen, Serge G
- Martin, Samia
- Mavilio, Fulvio
- Amirjanians, Vazrik
- Stieger, Knut
- Lorenz, Birgit
- Behar-Cohen, Francine
- Arsenijevic, Yvan
Producer: 20171002
In:
Translational research : the journal of laboratory and clinical medicine vol. 188
Availability: No items available.
|
|
|
53.
|
Transcriptional enhancers induce insertional gene deregulation independently from the vector type and design. [electronic resource] by
- Maruggi, Giulietta
- Porcellini, Simona
- Facchini, Giulia
- Perna, Serena K
- Cattoglio, Claudia
- Sartori, Daniela
- Ambrosi, Alessandro
- Schambach, Axel
- Baum, Christopher
- Bonini, Chiara
- Bovolenta, Chiara
- Mavilio, Fulvio
- Recchia, Alessandra
Producer: 20090629
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 17
Availability: No items available.
|
|
|
54.
|
Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency. [electronic resource] by
- Soheili, Tayebeh
- Durand, Amandine
- Sepulveda, Fernando E
- Rivière, Julie
- Lagresle-Peyrou, Chantal
- Sadek, Hanem
- de Saint Basile, Geneviève
- Martin, Samia
- Mavilio, Fulvio
- Cavazzana, Marina
- André-Schmutz, Isabelle
Publication details: Blood advances Dec 2017
In:
Blood advances vol. 1
Availability: No items available.
|
|
|
55.
|
Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem Cells. [electronic resource] by
- Poletti, Valentina
- Delli Carri, Alessia
- Malagoli Tagliazucchi, Guidantonio
- Faedo, Andrea
- Petiti, Luca
- Mazza, Emilia Maria Cristina
- Peano, Clelia
- De Bellis, Gianluca
- Bicciato, Silvio
- Miccio, Annarita
- Cattaneo, Elena
- Mavilio, Fulvio
Producer: 20160415
In:
PloS one vol. 10
Availability: No items available.
|
|
|
56.
|
Targeted gene addition in human epithelial stem cells by zinc-finger nuclease-mediated homologous recombination. [electronic resource] by
- Coluccio, Andrea
- Miselli, Francesca
- Lombardo, Angelo
- Marconi, Alessandra
- Malagoli Tagliazucchi, Guidantonio
- Gonçalves, Manuel A
- Pincelli, Carlo
- Maruggi, Giulietta
- Del Rio, Marcela
- Naldini, Luigi
- Larcher, Fernando
- Mavilio, Fulvio
- Recchia, Alessandra
Producer: 20140326
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 21
Availability: No items available.
|
|
|
57.
|
Hot spots of retroviral integration in human CD34+ hematopoietic cells. [electronic resource] by
- Cattoglio, Claudia
- Facchini, Giulia
- Sartori, Daniela
- Antonelli, Antonella
- Miccio, Annarita
- Cassani, Barbara
- Schmidt, Manfred
- von Kalle, Christof
- Howe, Steve
- Thrasher, Adrian J
- Aiuti, Alessandro
- Ferrari, Giuliana
- Recchia, Alessandra
- Mavilio, Fulvio
Producer: 20071030
In:
Blood vol. 110
Availability: No items available.
|
|
|
58.
|
Retroviral vector integration deregulates gene expression but has no consequence on the biology and function of transplanted T cells. [electronic resource] by
- Recchia, Alessandra
- Bonini, Chiara
- Magnani, Zulma
- Urbinati, Fabrizia
- Sartori, Daniela
- Muraro, Sara
- Tagliafico, Enrico
- Bondanza, Attilio
- Stanghellini, Maria Teresa Lupo
- Bernardi, Massimo
- Pescarollo, Alessandra
- Ciceri, Fabio
- Bordignon, Claudio
- Mavilio, Fulvio
Producer: 20060321
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 103
Availability: No items available.
|
|
|
59.
|
Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID. [electronic resource] by
- Charrier, Sabine
- Lagresle-Peyrou, Chantal
- Poletti, Valentina
- Rothe, Michael
- Cédrone, Grégory
- Gjata, Bernard
- Mavilio, Fulvio
- Fischer, Alain
- Schambach, Axel
- de Villartay, Jean-Pierre
- Cavazzana, Marina
- Hacein-Bey-Abina, Salima
- Galy, Anne
Publication details: Molecular therapy. Methods & clinical development Dec 2019
In:
Molecular therapy. Methods & clinical development vol. 15
Availability: No items available.
|
|
|
60.
|
Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapy. [electronic resource] by
- Cassani, Barbara
- Montini, Eugenio
- Maruggi, Giulietta
- Ambrosi, Alessandro
- Mirolo, Massimiliano
- Selleri, Silvia
- Biral, Erika
- Frugnoli, Ilaria
- Hernandez-Trujillo, Vivian
- Di Serio, Clelia
- Roncarolo, Maria Grazia
- Naldini, Luigi
- Mavilio, Fulvio
- Aiuti, Alessandro
Producer: 20091117
In:
Blood vol. 114
Availability: No items available.
|