Results
|
|
21.
|
Mouse neural progenitor cells differentiate into oligodendrocytes in the brain of a knockout mouse model of Canavan disease. [electronic resource] by
- Surendran, Sankar
- Shihabuddin, Lamya S
- Clarke, Jennifer
- Taksir, Tatyana V
- Stewart, Gregory R
- Parsons, Geoffrey
- Yang, Wendy
- Tyring, Stephen K
- Michals-Matalon, Kimberlee
- Matalon, Reuben
Producer: 20041221
In:
Brain research. Developmental brain research vol. 153
Availability: No items available.
|
|
|
22.
|
|
|
|
23.
|
Temporal neuropathologic and behavioral phenotype of 6neo/6neo Pompe disease mice. [electronic resource] by
- Sidman, Richard L
- Taksir, Tatyana
- Fidler, Jonathan
- Zhao, Michael
- Dodge, James C
- Passini, Marco A
- Raben, Nina
- Thurberg, Beth L
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20080924
In:
Journal of neuropathology and experimental neurology vol. 67
Availability: No items available.
|
|
|
24.
|
|
|
|
25.
|
Marked differences in neurochemistry and aggregates despite similar behavioural and neuropathological features of Huntington disease in the full-length BACHD and YAC128 mice. [electronic resource] by
- Pouladi, Mahmoud A
- Stanek, Lisa M
- Xie, Yuanyun
- Franciosi, Sonia
- Southwell, Amber L
- Deng, Yu
- Butland, Stefanie
- Zhang, Weining
- Cheng, Seng H
- Shihabuddin, Lamya S
- Hayden, Michael R
Producer: 20120913
In:
Human molecular genetics vol. 21
Availability: No items available.
|
|
|
26.
|
Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain. [electronic resource] by
- Sullivan, Jennifer A
- Stanek, Lisa M
- Lukason, Michael J
- Bu, Jie
- Osmond, Shayla R
- Barry, Elizabeth A
- O'Riordan, Catherine R
- Shihabuddin, Lamya S
- Cheng, Seng H
- Scaria, Abraham
Producer: 20181105
In:
Gene therapy vol. 25
Availability: No items available.
|
|
|
27.
|
Cerebrospinal fluid proteomics implicates the granin family in Parkinson's disease. [electronic resource] by
- Rotunno, Melissa S
- Lane, Monica
- Zhang, Wenfei
- Wolf, Pavlina
- Oliva, Petra
- Viel, Catherine
- Wills, Anne-Marie
- Alcalay, Roy N
- Scherzer, Clemens R
- Shihabuddin, Lamya S
- Zhang, Kate
- Sardi, S Pablo
Producer: 20201113
In:
Scientific reports vol. 10
Availability: No items available.
|
|
|
28.
|
Ability of adeno-associated virus serotype 8-mediated hepatic expression of acid alpha-glucosidase to correct the biochemical and motor function deficits of presymptomatic and symptomatic Pompe mice. [electronic resource] by
- Ziegler, Robin J
- Bercury, Scott D
- Fidler, Jonathan
- Zhao, Michael A
- Foley, Joseph
- Taksir, Tatyana V
- Ryan, Susan
- Hodges, Bradley L
- Scheule, Ronald K
- Shihabuddin, Lamya S
- Cheng, Seng H
Producer: 20080722
In:
Human gene therapy vol. 19
Availability: No items available.
|
|
|
29.
|
Metabolic signatures of amyotrophic lateral sclerosis reveal insights into disease pathogenesis. [electronic resource] by
- Dodge, James C
- Treleaven, Christopher M
- Fidler, Jonathan A
- Tamsett, Thomas J
- Bao, Channa
- Searles, Michelle
- Taksir, Tatyana V
- Misra, Kuma
- Sidman, Richard L
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20130906
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 110
Availability: No items available.
|
|
|
30.
|
Distribution of acid sphingomyelinase in rodent and non-human primate brain after intracerebroventricular infusion. [electronic resource] by
- Ziegler, Robin J
- Salegio, Ernesto A
- Dodge, James C
- Bringas, John
- Treleaven, Christopher M
- Bercury, Scott D
- Tamsett, Thomas J
- Shihabuddin, Lamya
- Hadaczek, Piotr
- Fiandaca, Massimo
- Bankiewicz, Krystof
- Scheule, Ronald K
Producer: 20111102
In:
Experimental neurology vol. 231
Availability: No items available.
|
|
|
31.
|
Glycosphingolipids are modulators of disease pathogenesis in amyotrophic lateral sclerosis. [electronic resource] by
- Dodge, James C
- Treleaven, Christopher M
- Pacheco, Joshua
- Cooper, Samantha
- Bao, Channa
- Abraham, Marissa
- Cromwell, Mandy
- Sardi, S Pablo
- Chuang, Wei-Lien
- Sidman, Richard L
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20151117
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 112
Availability: No items available.
|
|
|
32.
|
Gene transfer to the CNS is efficacious in immune-primed mice harboring physiologically relevant titers of anti-AAV antibodies. [electronic resource] by
- Treleaven, Christopher M
- Tamsett, Thomas J
- Bu, Jie
- Fidler, Jonathan A
- Sardi, S Pablo
- Hurlbut, Gregory D
- Woodworth, Lisa A
- Cheng, Seng H
- Passini, Marco A
- Shihabuddin, Lamya S
- Dodge, James C
Producer: 20130124
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 20
Availability: No items available.
|
|
|
33.
|
Widespread AAV1- and AAV2-mediated transgene expression in the nonhuman primate brain: implications for Huntington's disease. [electronic resource] by
- Hadaczek, Piotr
- Stanek, Lisa
- Ciesielska, Agnieszka
- Sudhakar, Vivek
- Samaranch, Lluis
- Pivirotto, Philip
- Bringas, John
- O'Riordan, Catherine
- Mastis, Bryan
- San Sebastian, Waldy
- Forsayeth, John
- Cheng, Seng H
- Bankiewicz, Krystof S
- Shihabuddin, Lamya S
Producer: 20160713
In:
Molecular therapy. Methods & clinical development vol. 3
Availability: No items available.
|
|
|
34.
|
Glucocerebrosidase modulates cognitive and motor activities in murine models of Parkinson's disease. [electronic resource] by
- Rockenstein, Edward
- Clarke, Jennifer
- Viel, Catherine
- Panarello, Nicholas
- Treleaven, Christopher M
- Kim, Changyoun
- Spencer, Brian
- Adame, Anthony
- Park, Hyejung
- Dodge, James C
- Cheng, Seng H
- Shihabuddin, Lamya S
- Masliah, E
- Sardi, S Pablo
Producer: 20170921
In:
Human molecular genetics vol. 25
Availability: No items available.
|
|
|
35.
|
Merits of combination cortical, subcortical, and cerebellar injections for the treatment of Niemann-Pick disease type A. [electronic resource] by
- Bu, Jie
- Ashe, Karen M
- Bringas, John
- Marshall, John
- Dodge, James C
- Cabrera-Salazar, Mario A
- Forsayeth, John
- Schuchman, Edward H
- Bankiewicz, Krystof S
- Cheng, Seng H
- Shihabuddin, Lamya S
- Passini, Marco A
Producer: 20130328
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 20
Availability: No items available.
|
|
|
36.
|
CNS expression of glucocerebrosidase corrects alpha-synuclein pathology and memory in a mouse model of Gaucher-related synucleinopathy. [electronic resource] by
- Sardi, S Pablo
- Clarke, Jennifer
- Kinnecom, Cathrine
- Tamsett, Thomas J
- Li, Lingyun
- Stanek, Lisa M
- Passini, Marco A
- Grabowski, Gregory A
- Schlossmacher, Michael G
- Sidman, Richard L
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20111003
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 108
Availability: No items available.
|
|
|
37.
|
AAV4-mediated expression of IGF-1 and VEGF within cellular components of the ventricular system improves survival outcome in familial ALS mice. [electronic resource] by
- Dodge, James C
- Treleaven, Christopher M
- Fidler, Jonathan A
- Hester, Mark
- Haidet, Amanda
- Handy, Chalonda
- Rao, Meghan
- Eagle, Amy
- Matthews, Jennifer C
- Taksir, Tatyana V
- Cheng, Seng H
- Shihabuddin, Lamya S
- Kaspar, Brian K
Producer: 20110418
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 18
Availability: No items available.
|
|
|
38.
|
Intracerebroventricular infusion of acid sphingomyelinase corrects CNS manifestations in a mouse model of Niemann-Pick A disease. [electronic resource] by
- Dodge, James C
- Clarke, Jennifer
- Treleaven, Christopher M
- Taksir, Tatyana V
- Griffiths, Denise A
- Yang, Wendy
- Fidler, Jonathan A
- Passini, Marco A
- Karey, Kenneth P
- Schuchman, Edward H
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20090408
In:
Experimental neurology vol. 215
Availability: No items available.
|
|
|
39.
|
AAV vector-mediated correction of brain pathology in a mouse model of Niemann-Pick A disease. [electronic resource] by
- Passini, Marco A
- Macauley, Shannon L
- Huff, Michael R
- Taksir, Tatyana V
- Bu, Jie
- Wu, I-Huan
- Piepenhagen, Peter A
- Dodge, James C
- Shihabuddin, Lamya S
- O'Riordan, Catherine R
- Schuchman, Edward H
- Stewart, Gregory R
Producer: 20050727
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 11
Availability: No items available.
|
|
|
40.
|
Glucosylceramide synthase inhibition alleviates aberrations in synucleinopathy models. [electronic resource] by
- Sardi, S Pablo
- Viel, Catherine
- Clarke, Jennifer
- Treleaven, Christopher M
- Richards, Amy M
- Park, Hyejung
- Olszewski, Maureen A
- Dodge, James C
- Marshall, John
- Makino, Elina
- Wang, Bing
- Sidman, Richard L
- Cheng, Seng H
- Shihabuddin, Lamya S
Producer: 20180418
In:
Proceedings of the National Academy of Sciences of the United States of America vol. 114
Availability: No items available.
|