Results
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21.
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22.
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CD7-edited T cells expressing a CD7-specific CAR for the therapy of T-cell malignancies. [electronic resource] by
- Gomes-Silva, Diogo
- Srinivasan, Madhuwanti
- Sharma, Sandhya
- Lee, Ciaran M
- Wagner, Dimitrios L
- Davis, Timothy H
- Rouce, Rayne H
- Bao, Gang
- Brenner, Malcolm K
- Mamonkin, Maksim
Producer: 20170816
In:
Blood vol. 130
Availability: No items available.
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23.
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AAV-CRISPR Gene Editing Is Negated by Pre-existing Immunity to Cas9. [electronic resource] by
- Li, Ang
- Tanner, Mark R
- Lee, Ciaran M
- Hurley, Ayrea E
- De Giorgi, Marco
- Jarrett, Kelsey E
- Davis, Timothy H
- Doerfler, Alexandria M
- Bao, Gang
- Beeton, Christine
- Lagor, William R
Producer: 20210602
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 28
Availability: No items available.
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24.
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A Self-Deleting AAV-CRISPR System for [electronic resource] by
- Li, Ang
- Lee, Ciaran M
- Hurley, Ayrea E
- Jarrett, Kelsey E
- De Giorgi, Marco
- Lu, Weiqi
- Balderrama, Karol S
- Doerfler, Alexandria M
- Deshmukh, Harshavardhan
- Ray, Anirban
- Bao, Gang
- Lagor, William R
Publication details: Molecular therapy. Methods & clinical development Mar 2019
In:
Molecular therapy. Methods & clinical development vol. 12
Availability: No items available.
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25.
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Highly efficient editing of the β-globin gene in patient-derived hematopoietic stem and progenitor cells to treat sickle cell disease. [electronic resource] by
- Park, So Hyun
- Lee, Ciaran M
- Dever, Daniel P
- Davis, Timothy H
- Camarena, Joab
- Srifa, Waracharee
- Zhang, Yankai
- Paikari, Alireza
- Chang, Alicia K
- Porteus, Matthew H
- Sheehan, Vivien A
- Bao, Gang
Producer: 20191209
In:
Nucleic acids research vol. 47
Availability: No items available.
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26.
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Somatic genome editing with CRISPR/Cas9 generates and corrects a metabolic disease. [electronic resource] by
- Jarrett, Kelsey E
- Lee, Ciaran M
- Yeh, Yi-Hsien
- Hsu, Rachel H
- Gupta, Rajat
- Zhang, Min
- Rodriguez, Perla J
- Lee, Chang Seok
- Gillard, Baiba K
- Bissig, Karl-Dimiter
- Pownall, Henry J
- Martin, James F
- Bao, Gang
- Lagor, William R
Producer: 20181211
In:
Scientific reports vol. 7
Availability: No items available.
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27.
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Therapeutically relevant engraftment of a CRISPR-Cas9-edited HSC-enriched population with HbF reactivation in nonhuman primates. [electronic resource] by
- Humbert, Olivier
- Radtke, Stefan
- Samuelson, Clare
- Carrillo, Ray R
- Perez, Anai M
- Reddy, Sowmya S
- Lux, Christopher
- Pattabhi, Sowmya
- Schefter, Lauren E
- Negre, Olivier
- Lee, Ciaran M
- Bao, Gang
- Adair, Jennifer E
- Peterson, Christopher W
- Rawlings, David J
- Scharenberg, Andrew M
- Kiem, Hans-Peter
Producer: 20200727
In:
Science translational medicine vol. 11
Availability: No items available.
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28.
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A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells. [electronic resource] by
- Vakulskas, Christopher A
- Dever, Daniel P
- Rettig, Garrett R
- Turk, Rolf
- Jacobi, Ashley M
- Collingwood, Michael A
- Bode, Nicole M
- McNeill, Matthew S
- Yan, Shuqi
- Camarena, Joab
- Lee, Ciaran M
- Park, So Hyun
- Wiebking, Volker
- Bak, Rasmus O
- Gomez-Ospina, Natalia
- Pavel-Dinu, Mara
- Sun, Wenchao
- Bao, Gang
- Porteus, Matthew H
- Behlke, Mark A
Producer: 20190510
In:
Nature medicine vol. 24
Availability: No items available.
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29.
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High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia. [electronic resource] by
- Vaidyanathan, Sriram
- Salahudeen, Ameen A
- Sellers, Zachary M
- Bravo, Dawn T
- Choi, Shannon S
- Batish, Arpit
- Le, Wei
- Baik, Ron
- de la O, Sean
- Kaushik, Milan P
- Galper, Noah
- Lee, Ciaran M
- Teran, Christopher A
- Yoo, Jessica H
- Bao, Gang
- Chang, Eugene H
- Patel, Zara M
- Hwang, Peter H
- Wine, Jeffrey J
- Milla, Carlos E
- Desai, Tushar J
- Nayak, Jayakar V
- Kuo, Calvin J
- Porteus, Matthew H
Producer: 20210427
In:
Cell stem cell vol. 26
Availability: No items available.
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