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Suitability Of Nitisinone In Alkaptonuria 1 (SONIA 1): an international, multicentre, randomised, open-label, no-treatment controlled, parallel-group, dose-response study to investigate the effect of once daily nitisinone on 24-h urinary homogentisic acid excretion in patients with alkaptonuria after 4 weeks of treatment. [electronic resource] by
- Ranganath, Lakshminarayan R
- Milan, Anna M
- Hughes, Andrew T
- Dutton, John J
- Fitzgerald, Richard
- Briggs, Michael C
- Bygott, Helen
- Psarelli, Eftychia E
- Cox, Trevor F
- Gallagher, James A
- Jarvis, Jonathan C
- van Kan, Christa
- Hall, Anthony K
- Laan, Dinny
- Olsson, Birgitta
- Szamosi, Johan
- Rudebeck, Mattias
- Kullenberg, Torbjörn
- Cronlund, Arvid
- Svensson, Lennart
- Junestrand, Carin
- Ayoob, Hana
- Timmis, Oliver G
- Sireau, Nicolas
- Le Quan Sang, Kim-Hanh
- Genovese, Federica
- Braconi, Daniela
- Santucci, Annalisa
- Nemethova, Martina
- Zatkova, Andrea
- McCaffrey, Judith
- Christensen, Peter
- Ross, Gordon
- Imrich, Richard
- Rovensky, Jozef
Producer: 20160628
In:
Annals of the rheumatic diseases vol. 75
Availability: No items available.
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