Nadler, H L

Current status of treatment in storage disorders. [electronic resource] - Birth defects original article series 1976 - 177-88 p. digital

Publication Type: Journal Article; Review

0547-6844


Animals
Aspergillus niger
Cerebroside-Sulfatase--therapeutic use
Child, Preschool
Cystinosis--surgery
Enzyme Induction
Fabry Disease--therapy
Gangliosidoses--therapy
Gaucher Disease--therapy
Glucosidases--therapeutic use
Glucuronidase--therapeutic use
Glycogen Storage Disease--surgery
Hepatolenticular Degeneration--surgery
Humans
Kidney Transplantation
Leukodystrophy, Metachromatic--therapy
Liver Transplantation
Metabolism, Inborn Errors--therapy
Mucopolysaccharidoses--therapy
Niemann-Pick Diseases--surgery
Portacaval Shunt, Surgical
Transplantation, Homologous