Novo, F J Gene transfer and expression of human alpha-galactosidase from mouse muscle in vitro and in vivo. [electronic resource] - Gene therapy May 1997 - 488-92 p. digital Publication Type: Journal Article; Research Support, Non-U.S. Gov't ISSN: 0969-7128 Standard No.: 10.1038/sj.gt.3300410 doi Subjects--Topical Terms: AnimalsCell LineCells, CulturedFibroblasts--metabolismGene ExpressionGene Transfer TechniquesGenetic Therapy--methodsGenetic VectorsHumansInjections, IntramuscularLysosomal Storage Diseases--therapyLysosomes--enzymologyMiceMuscle, Skeletal--enzymologyPlasmidsReceptor, IGF Type 2--metabolismalpha-Galactosidase--genetics