Novo, F J

Gene transfer and expression of human alpha-galactosidase from mouse muscle in vitro and in vivo. [electronic resource] - Gene therapy May 1997 - 488-92 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

0969-7128

10.1038/sj.gt.3300410 doi


Animals
Cell Line
Cells, Cultured
Fibroblasts--metabolism
Gene Expression
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Humans
Injections, Intramuscular
Lysosomal Storage Diseases--therapy
Lysosomes--enzymology
Mice
Muscle, Skeletal--enzymology
Plasmids
Receptor, IGF Type 2--metabolism
alpha-Galactosidase--genetics