Dorin, J R

A demonstration using mouse models that successful gene therapy for cystic fibrosis requires only partial gene correction. [electronic resource] - Gene therapy Sep 1996 - 797-801 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

0969-7128


Animals
Chlorides--metabolism
Colforsin--pharmacology
Crosses, Genetic
Cystic Fibrosis--metabolism
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
Electric Conductivity
Gene Expression
Genes, Recessive--genetics
Genetic Therapy--methods
Genotype
Intestines--chemistry
Mice
Mice, Mutant Strains
Phenotype
RNA, Messenger--analysis