Bone marrow transplantation in Batten disease (neuronal ceroid-lipofuscinosis). Will it work? Preliminary studies on coculture experiments and on bone marrow transplant in late infantile Batten disease. [electronic resource]
- American journal of medical genetics Jun 1995
- 369-73 p. digital
Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't
0148-7299
10.1002/ajmg.1320570253 doi
Bone Marrow Transplantation Cells, Cultured Child, Preschool Female Humans Inclusion Bodies--pathology Infant Intestinal Mucosa--pathology Lymphocyte Activation Lymphocytes--immunology Male Microscopy, Electron Mitogens Muscle, Smooth--pathology Neuronal Ceroid-Lipofuscinoses--immunology Rectum--pathology Skin--pathology