TY  - GEN
AU  - Grossman,M
AU  - Rader,D J
AU  - Muller,D W
AU  - Kolansky,D M
AU  - Kozarsky,K
AU  - Clark,B J
AU  - Stein,E A
AU  - Lupien,P J
AU  - Brewer,H B
AU  - Raper,S E
TI  - A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia
SN  - 1078-8956
PY  - 1995///1228
KW  - Adult
KW  - Antibody Formation
KW  - Cell Transplantation
KW  - Cells, Cultured
KW  - Child
KW  - Cholesterol
KW  - blood
KW  - Female
KW  - Follow-Up Studies
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - Heterozygote
KW  - Humans
KW  - Hyperlipoproteinemia Type II
KW  - therapy
KW  - In Situ Hybridization
KW  - Lipids
KW  - Lipoproteins, LDL
KW  - Liver
KW  - cytology
KW  - Male
KW  - Pilot Projects
KW  - Receptors, LDL
KW  - genetics
KW  - Treatment Outcome
N1  - Publication Type: Clinical Trial; Journal Article; Research Support, U.S. Gov't, P.H.S
UR  - https://doi.org/10.1038/nm1195-1148
ER  -