Grossman, M <br/><br/>
A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia.  [electronic resource] 

 -  Nature medicine  Nov 1995 
 - 1148-54 p.  digital 
<br/><br/> Publication Type: Clinical Trial; Journal Article; Research Support, U.S. Gov't, P.H.S. 
<br/><br/><label>ISSN: </label>1078-8956 
<br/><br/><label>Standard No.: </label>10.1038/nm1195-1148  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Adult<br/>Antibody Formation<br/>Cell Transplantation<br/>Cells, Cultured<br/>Child<br/>Cholesterol--blood<br/>Female<br/>Follow-Up Studies<br/>Gene Transfer Techniques<br/>Genetic Therapy--methods<br/>Genetic Vectors<br/>Heterozygote<br/>Humans<br/>Hyperlipoproteinemia Type II--therapy<br/>In Situ Hybridization<br/>Lipids--blood<br/>Lipoproteins, LDL--blood<br/>Liver--cytology<br/>Male<br/>Pilot Projects<br/>Receptors, LDL--genetics<br/>Treatment Outcome