Fischer, M Dominik

Safety and Vision Outcomes of Subretinal Gene Therapy Targeting Cone Photoreceptors in Achromatopsia: A Nonrandomized Controlled Trial. [electronic resource] - JAMA ophthalmology 06 2020 - 643-651 p. digital

Publication Type: Controlled Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't

2168-6173

10.1001/jamaophthalmol.2020.1032 doi


Adult
Color Vision Defects--diagnosis
Cyclic Nucleotide-Gated Cation Channels--genetics
Electroretinography
Female
Follow-Up Studies
Genetic Therapy--methods
Humans
Male
Middle Aged
Retina
Retinal Cone Photoreceptor Cells--pathology
Retrospective Studies
Treatment Outcome
Visual Acuity
Young Adult