Early data on long-term efficacy and safety of inotersen in patients with hereditary transthyretin amyloidosis: a 2-year update from the open-label extension of the NEURO-TTR trial. [electronic resource]
- European journal of neurology 08 2020
- 1374-1381 p. digital
Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't
1468-1331
10.1111/ene.14285 doi
Amyloid Neuropathies, Familial--drug therapy Female Humans Male Middle Aged Oligonucleotides Prealbumin Quality of Life