TY  - GEN
AU  - Kurkiewicz,Adam
AU  - Cooper,Anneli
AU  - McIlwaine,Emily
AU  - Cumming,Sarah A
AU  - Adam,Berit
AU  - Krahe,Ralf
AU  - Puymirat,Jack
AU  - Schoser,Benedikt
AU  - Timchenko,Lubov
AU  - Ashizawa,Tetsuo
AU  - Thornton,Charles A
AU  - Rogers,Simon
AU  - McClure,John D
AU  - Monckton,Darren G
TI  - Towards development of a statistical framework to evaluate myotonic dystrophy type 1 mRNA biomarkers in the context of a clinical trial
SN  - 1932-6203
PY  - 2020///0710
KW  - Alternative Splicing
KW  - Biostatistics
KW  - Clinical Trials as Topic
KW  - methods
KW  - Databases, Nucleic Acid
KW  - statistics & numerical data
KW  - Genetic Markers
KW  - Humans
KW  - Least-Squares Analysis
KW  - Machine Learning
KW  - Models, Genetic
KW  - Muscles
KW  - metabolism
KW  - Myotonic Dystrophy
KW  - genetics
KW  - Myotonin-Protein Kinase
KW  - Oligonucleotide Array Sequence Analysis
KW  - Polyadenylation
KW  - RNA, Messenger
KW  - Treatment Outcome
KW  - Trinucleotide Repeat Expansion
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1371/journal.pone.0231000
ER  -