Kurkiewicz, Adam <br/><br/>
Towards development of a statistical framework to evaluate myotonic dystrophy type 1 mRNA biomarkers in the context of a clinical trial.  [electronic resource] 

 -  PloS one  2020 
 - e0231000 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1932-6203 
<br/><br/><label>Standard No.: </label>10.1371/journal.pone.0231000  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Alternative Splicing<br/>Biostatistics<br/>Clinical Trials as Topic--methods<br/>Databases, Nucleic Acid--statistics & numerical data<br/>Genetic Markers<br/>Humans<br/>Least-Squares Analysis<br/>Machine Learning<br/>Models, Genetic<br/>Muscles--metabolism<br/>Myotonic Dystrophy--genetics<br/>Myotonin-Protein Kinase--genetics<br/>Oligonucleotide Array Sequence Analysis--statistics & numerical data<br/>Polyadenylation<br/>RNA, Messenger--genetics<br/>Treatment Outcome<br/>Trinucleotide Repeat Expansion