Kakkis, Emil <br/><br/>
Urinary glycosaminoglycans as a potential biomarker for evaluating treatment efficacy in subjects with mucopolysaccharidoses.  [electronic resource] 

 -  Molecular genetics and metabolism  05 2020 
 - 7-15 p.  digital 
<br/><br/> Publication Type: Journal Article; Review 
<br/><br/><label>ISSN: </label>1096-7206 
<br/><br/><label>Standard No.: </label>10.1016/j.ymgme.2020.02.006  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Biomarkers--metabolism<br/>Enzyme Replacement Therapy<br/>Glycosaminoglycans--metabolism<br/>Humans<br/>Mucopolysaccharidoses--enzymology<br/>Treatment Outcome