TY  - GEN
AU  - Wang,Raymond Y
AU  - da Silva Franco,José Francisco
AU  - López-Valdez,Jaime
AU  - Martins,Esmeralda
AU  - Sutton,Vernon Reid
AU  - Whitley,Chester B
AU  - Zhang,Lin
AU  - Cimms,Tricia
AU  - Marsden,Deborah
AU  - Jurecka,Agnieszka
AU  - Harmatz,Paul
TI  - The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII
SN  - 1096-7206
PY  - 2020///1123
KW  - Adolescent
KW  - Adult
KW  - Antibodies, Neutralizing
KW  - Blood-Brain Barrier
KW  - drug effects
KW  - Child
KW  - Cross-Over Studies
KW  - Enzyme Replacement Therapy
KW  - Female
KW  - Glucuronidase
KW  - administration & dosage
KW  - Glycosaminoglycans
KW  - urine
KW  - Humans
KW  - Male
KW  - Mucopolysaccharidosis VII
KW  - drug therapy
KW  - Rare Diseases
KW  - therapy
KW  - Treatment Outcome
N1  - Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1016/j.ymgme.2020.01.003
ER  -