Combinatorial treatment for spinal muscular atrophy: An Editorial for 'Combined treatment with the histone deacetylase inhibitor LBH589 and a splice-switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells' on page 264. [electronic resource]
- Journal of neurochemistry 04 2020
- 146-149 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't; Comment
1471-4159
10.1111/jnc.14974 doi
Animals Histone Deacetylase Inhibitors Humans Muscular Atrophy, Spinal Oligonucleotides, Antisense Panobinostat RNA Splicing Survival of Motor Neuron 2 Protein