Mercuri, Eugenio <br/><br/>
Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study.  [electronic resource] 

 -  Journal of comparative effectiveness research  04 2020 
 - 341-360 p.  digital 
<br/><br/> Publication Type: Journal Article; Multicenter Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S. 
<br/><br/><label>ISSN: </label>2042-6313 
<br/><br/><label>Standard No.: </label>10.2217/cer-2019-0171  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Codon, Nonsense--genetics<br/>Dystrophin--genetics<br/>Humans<br/>Muscular Dystrophy, Duchenne--drug therapy<br/>Oxadiazoles--adverse effects<br/>Registries<br/>Treatment Outcome