Moretti, A <br/><br/>
Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy.  [electronic resource] 

 -  Nature medicine  02 2020 
 - 207-214 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1546-170X 
<br/><br/><label>Standard No.: </label>10.1038/s41591-019-0738-2  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Disease Models, Animal<br/>Dystrophin--genetics<br/>Exons<br/>Female<br/>Frameshift Mutation<br/>Gene Editing--methods<br/>Gene Expression Regulation<br/>Genetic Therapy<br/>Genome<br/>Heart Failure--genetics<br/>Humans<br/>Induced Pluripotent Stem Cells--cytology<br/>Male<br/>Mass Spectrometry<br/>Muscle, Skeletal--metabolism<br/>Muscles--metabolism<br/>Muscular Dystrophy, Duchenne--genetics<br/>Myoblasts--metabolism<br/>Myocytes, Cardiac--metabolism<br/>Proteome<br/>Swine<br/>RNA, Guide, CRISPR-Cas Systems