Discontinuation of enzyme replacement therapy in adults with Pompe disease: Evaluating the European POmpe Consortium stop criteria. [electronic resource]
- Neuromuscular disorders : NMD 01 2020
- 59-66 p. digital
Adult Aged Aged, 80 and over Clinical Decision-Making Enzyme Replacement Therapy--adverse effects Female Glycogen Storage Disease Type II--drug therapy Humans Male Middle Aged Netherlands Outcome and Process Assessment, Health Care Practice Guidelines as Topic--standards Prospective Studies