van Kooten, H A

Discontinuation of enzyme replacement therapy in adults with Pompe disease: Evaluating the European POmpe Consortium stop criteria. [electronic resource] - Neuromuscular disorders : NMD 01 2020 - 59-66 p. digital

Publication Type: Evaluation Study; Journal Article

1873-2364

10.1016/j.nmd.2019.11.007 doi


Adult
Aged
Aged, 80 and over
Clinical Decision-Making
Enzyme Replacement Therapy--adverse effects
Female
Glycogen Storage Disease Type II--drug therapy
Humans
Male
Middle Aged
Netherlands
Outcome and Process Assessment, Health Care
Practice Guidelines as Topic--standards
Prospective Studies