Landfeldt, Erik <br/><br/>
Improvements in health status and utility associated with ataluren for the treatment of nonsense mutation Duchenne muscular dystrophy.  [electronic resource] 

 -  Muscle & nerve  03 2020 
 - 363-368 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>1097-4598 
<br/><br/><label>Standard No.: </label>10.1002/mus.26787  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Codon, Nonsense<br/>Delphi Technique<br/>Health Status<br/>Humans<br/>Muscular Dystrophy, Duchenne--drug therapy<br/>Oxadiazoles--therapeutic use<br/>Treatment Outcome