A Safe and Reliable Technique for CNS Delivery of AAV Vectors in the Cisterna Magna. [electronic resource]
- Molecular therapy : the journal of the American Society of Gene Therapy 02 2020
- 411-421 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0024
10.1016/j.ymthe.2019.11.012 doi
Animals Catheters Central Nervous System--metabolism Cisterna Magna--metabolism Dependovirus--genetics Gene Expression Gene Transfer Techniques Genes, Reporter Genetic Therapy Genetic Vectors--administration & dosage Humans Injections, Spinal Magnetic Resonance Imaging Models, Animal Sheep Surgery, Computer-Assisted Tomography, X-Ray Computed Transduction, Genetic Transgenes Video Recording