TY  - GEN
AU  - Salabarria,S M
AU  - Nair,J
AU  - Clement,N
AU  - Smith,B K
AU  - Raben,N
AU  - Fuller,D D
AU  - Byrne,B J
AU  - Corti,M
TI  - Advancements in AAV-mediated Gene Therapy for Pompe Disease
SN  - 2214-3602
PY  - 2020///1013
KW  - Animals
KW  - Dependovirus
KW  - Genetic Therapy
KW  - Glycogen Storage Disease Type II
KW  - therapy
KW  - Humans
N1  - Publication Type: Journal Article; Review
UR  - https://doi.org/10.3233/JND-190426
ER  -