Salabarria, S M <br/><br/>
Advancements in AAV-mediated Gene Therapy for Pompe Disease.  [electronic resource] 

 -  Journal of neuromuscular diseases  2020 
 - 15-31 p.  digital 
<br/><br/> Publication Type: Journal Article; Review 
<br/><br/><label>ISSN: </label>2214-3602 
<br/><br/><label>Standard No.: </label>10.3233/JND-190426  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Dependovirus<br/>Genetic Therapy<br/>Glycogen Storage Disease Type II--therapy<br/>Humans