Heijerman, Harry G M

Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial. [electronic resource] - Lancet (London, England) 11 2019 - 1940-1948 p. digital

Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1474-547X

10.1016/S0140-6736(19)32597-8 doi


Adolescent
Aminophenols--administration & dosage
Benzodioxoles--administration & dosage
Child
Chloride Channel Agonists--administration & dosage
Cystic Fibrosis--drug therapy
Cystic Fibrosis Transmembrane Conductance Regulator--genetics
Double-Blind Method
Drug Therapy, Combination
Female
Humans
Indoles--administration & dosage
Male
Pyrazoles--administration & dosage
Pyridines--administration & dosage
Pyrrolidines--administration & dosage
Quinolones--administration & dosage
Sweat--chemistry