Khayat, Delia

The changing landscape of clinical trials for mitochondrial diseases: 2011 to present. [electronic resource] - Mitochondrion 01 2020 - 51-57 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Review

1872-8278

10.1016/j.mito.2019.10.010 doi


Genetic Therapy
Humans
Mitochondrial Diseases--diagnosis
Orphan Drug Production
Rare Diseases--genetics
Research Design