Individualized treatment with denosumab in children with osteogenesis imperfecta - follow up of a trial cohort. [electronic resource]
- Orphanet journal of rare diseases 09 2019
- 219 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1750-1172
10.1186/s13023-019-1197-z doi
Bone Density--drug effects Bone Density Conservation Agents--therapeutic use Child Collagen Type I--genetics Collagen Type I, alpha 1 Chain Denosumab--therapeutic use Diphosphonates--therapeutic use Female Follow-Up Studies Humans Hypercalciuria--drug therapy Male Mutation--genetics Osteogenesis Imperfecta--drug therapy Retrospective Studies