Complement and inflammasome overactivation mediates paroxysmal nocturnal hemoglobinuria with autoinflammation. [electronic resource]
- The Journal of clinical investigation 12 2019
- 5123-5136 p. digital
Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't
1558-8238
10.1172/JCI123501 doi
Aged Alleles Antibodies, Monoclonal, Humanized--therapeutic use Complement System Proteins--immunology Female Gene Deletion Genes, X-Linked Germany Glycosylphosphatidylinositols--metabolism Hemoglobinuria, Paroxysmal--immunology Hemolysis--drug effects Humans Inflammasomes--immunology Inflammation--immunology Japan Leukocytes--immunology Male Membrane Proteins--genetics Middle Aged Mutation Point Mutation THP-1 Cells