TY - GEN AU - Hetzel,Miriam AU - Lopez-Rodriguez,Elena AU - Mucci,Adele AU - Nguyen,Ariane Hai Ha AU - Suzuki,Takuji AU - Shima,Kenjiro AU - Buchegger,Theresa AU - Dettmer,Sabine AU - Rodt,Thomas AU - Bankstahl,Jens P AU - Malik,Punam AU - Knudsen,Lars AU - Schambach,Axel AU - Hansen,Gesine AU - Trapnell,Bruce C AU - Lachmann,Nico AU - Moritz,Thomas TI - Effective hematopoietic stem cell-based gene therapy in a murine model of hereditary pulmonary alveolar proteinosis SN - 1592-8721 PY - 2021///0427 KW - Animals KW - Disease Models, Animal KW - Genetic Therapy KW - Hematopoietic Stem Cells KW - Macrophages, Alveolar KW - Mice KW - Pulmonary Alveolar Proteinosis KW - genetics N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.3324/haematol.2018.214866 ER -